Patisiran |
SAR-438037; GENZ-438027; ALN-TTR02; ALN-18328 |
Approved |
Alnylam Pharmaceuticals Inc |
Onpattro |
United States |
Amyloid Neuropathies, Familial |
Alnylam Pharmaceuticals Inc |
2018-08-10 |
Amyloidosis, Familial; Amyloid Neuropathies, Familial; Polyneuropathies; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis; Amyloid Neuropathies |
Details
|
Vutrisiran |
ALN-TTRSC02 |
Approved |
Alnylam Pharmaceuticals Inc |
AMVUTTRA |
United States |
Amyloid Neuropathies, Familial; Transthyretin amyloidosis |
Alnylam Pharmaceuticals Inc |
2022-06-13 |
Amyloidosis, Familial; Amyloid Neuropathies, Familial; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis |
Details
|
Inotersen sodium |
ISIS-420915; GSK-2998728 |
Approved |
Ionis Pharmaceuticals Inc |
Tegsedi |
EU |
Amyloidosis |
Akcea Therapeutics Ireland Ltd |
2018-07-05 |
Amyloid Neuropathies, Familial; Adenomatous Polyposis Coli; Amyloidosis; Transthyretin amyloidosis |
Details
|
Tafamidis |
PF-6291826; Fx-1006A; PF-06291826; FX-1006A |
Approved |
Pfizer Inc |
维万心, VYNDAMAX |
United States |
Heart Diseases |
Foldrx Pharmaceuticals Inc |
2019-05-03 |
Heart Diseases; Transthyretin amyloidosis |
Details
|
Eplontersen |
ION-682884; ION-TTR-LRx; IONIS-TTR-LRx; AKCEA-TTR-LRx |
Approved |
Ionis Pharmaceuticals Inc |
WAINUA |
United States |
Transthyretin amyloidosis |
Astrazeneca Ab |
2023-12-21 |
Amyloid Neuropathies, Familial; Cardiomyopathies; Transthyretin amyloidosis |
Details
|
Tafamidis Meglumine |
FX-1006A; PF-6291826; Fx-1006A; PF-06291826 |
Approved |
Pfizer Inc |
维达全, Vyndaqel |
EU |
Amyloidosis |
Pfizer Europe Ma Eeig |
2011-11-16 |
Amyloid Neuropathies, Familial; Immunoglobulin Light-chain Amyloidosis; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis; Amyloid Neuropathies |
Details
|